{"id":3826,"date":"2021-09-13T08:40:48","date_gmt":"2021-09-13T12:40:48","guid":{"rendered":"https:\/\/www.gensight-biologics.com\/clinical-trials-in-rare-diseases-conference-2021-europe-and-usa-virtual-conference-2\/"},"modified":"2026-07-15T15:58:12","modified_gmt":"2026-07-15T19:58:12","slug":"clinical-trials-in-rare-diseases-conference-2021-europe-and-usa-virtual-conference","status":"publish","type":"post","link":"https:\/\/www.gensight-biologics.com\/fr\/2021\/09\/13\/clinical-trials-in-rare-diseases-conference-2021-europe-and-usa-virtual-conference\/","title":{"rendered":"Clinical Trials in Rare Diseases Conference 2021, Europe and USA, conf\u00e9rence virtuelle"},"content":{"rendered":"\nAvec plus de 40 fournisseurs de solutions, la conf\u00e9rence virtuelle sur <strong><a href=\"https:\/\/www.arena-international.com\/ctrdiseases\/agenda\" target=\"_blank\" rel=\"noopener\">les essais cliniques dans les maladies rares 2021<\/a><\/strong> sera une plate-forme id\u00e9ale pour renouer avec les partenaires commerciaux actuels, rencontrer de nouveaux fournisseurs et d\u00e9couvrir quelles nouvelles technologies sont utilis\u00e9es pour am\u00e9liorer les essais cliniques sur les maladies rares.\n\nLe Dr Magali Taiel, Directeur M\u00e9dical, fera une pr\u00e9sentation orale sur notre produit candidat phare LUMEVOQ\u00ae (GS010\u00a0; lenadogene nolparvovec) comme d\u00e9taill\u00e9 ci-dessous\u00a0:\n\n&nbsp;\n\n<strong><u>Tuesday 14<sup>th<\/sup> September 2021<\/u><\/strong>\n\nHeure:\u00a0 9:00am \u2013 9:30am CET (heure locale de Paris)\n\n<span style=\"color: #33bdbc\"><strong>Rare disease in clinical development: learnings from development of Lumevoq Gene Therapy in Leber Hereditary Optic Neuropathy (LHON)<\/strong><\/span>\n<ul>\n \t<li>Overview: key aspects of Lumevoq Gene Therapy development<\/li>\n \t<li>Regulatory pathways and challenges around documentation and working with regulatory authorities<\/li>\n \t<li>Recruiting and following up with patients in order to maximise patient numbers and minimise attrition throughout the study<\/li>\n \t<li>Key learnings and takeaways: what do you need to know when running a gene therapy study?<\/li>\n<\/ul>\n","protected":false},"excerpt":{"rendered":"<p>Avec plus de 40 fournisseurs de solutions, la conf\u00e9rence virtuelle sur les essais cliniques dans les maladies rares 2021 sera une plate-forme id\u00e9ale pour renouer avec les partenaires commerciaux actuels, rencontrer de nouveaux fournisseurs et d\u00e9couvrir quelles nouvelles technologies sont utilis\u00e9es pour am\u00e9liorer les essais cliniques sur les maladies rares. Le Dr Magali Taiel, Directeur [&hellip;]<\/p>\n","protected":false},"author":4,"featured_media":0,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[55],"tags":[],"featured-area":[],"news-topic":[73,79],"news-type":[74,75,77],"post-year":[],"class_list":["post-3826","post","type-post","status-publish","format-standard","hentry","category-evenements","news-topic-gs010-lumevoq","news-topic-company-and-personnel","news-type-product-candidates","news-type-clinical","news-type-conferences"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Clinical Trials in Rare Diseases Conference 2021, Europe and USA, conf\u00e9rence virtuelle - GenSight Biologics<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.gensight-biologics.com\/fr\/2021\/09\/13\/clinical-trials-in-rare-diseases-conference-2021-europe-and-usa-virtual-conference\/\" \/>\n<meta property=\"og:locale\" content=\"fr_FR\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Clinical Trials in Rare Diseases Conference 2021, Europe and USA, conf\u00e9rence virtuelle - GenSight Biologics\" \/>\n<meta property=\"og:description\" content=\"Avec plus de 40 fournisseurs de solutions, la conf\u00e9rence virtuelle sur les essais cliniques dans les maladies rares 2021 sera une plate-forme id\u00e9ale pour renouer avec les partenaires commerciaux actuels, rencontrer de nouveaux fournisseurs et d\u00e9couvrir quelles nouvelles technologies sont utilis\u00e9es pour am\u00e9liorer les essais cliniques sur les maladies rares. 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